Stem Cell and Regenerative Medicine

Cell and Gene Therapy

Cells are the essential building blocks of all living things, and genes are often found deep within cells. Genes are small sections of DNA that carry genetic information and directions for creating proteins, which help build and maintain the body. Every person has around 20,000 genes and two copies of every one of their genes one from each parent. Small variations in genes end in differences in people’s appearance and, potentially, health. Genetic diseases happen when a critical piece or whole section of DNA is substituted, deleted, or duplicated. These changes are called hereditary mutations. Some genetic severe diseases caused by genetic mutations are often passed to future generations.

• AAV-based therapies
• CAR-T cell therapies
• CRISPR-based technologies
• Gene regulation therapies